MPS II
Showing 1 - 25 of >10,000
Mucopolysaccharidosis II Trial in Cincinnati (DNL310)
Enrolling by invitation
- Mucopolysaccharidosis II
-
Cincinnati, OhioCincinnati Children's Hospital Medical Center
Oct 10, 2023
MPS II Immunophenotyping
Recruiting
- MPS II
- +2 more
-
Durham, North CarolinaDuke University
Jun 3, 2022
Mucopolysaccharidosis Type II (MPS II) Trial in Oakland, Montréal (RGX-121)
Recruiting
- Mucopolysaccharidosis Type II (MPS II)
- RGX-121
-
Oakland, California
- +1 more
Oct 6, 2022
Mucopolysaccharidosis Type II (MPS II) Trial in Brazil, United States (RGX-121)
Recruiting
- Mucopolysaccharidosis Type II (MPS II)
- RGX-121
-
Oakland, California
- +4 more
Dec 22, 2022
Mucopolysaccharidosis (MPS), Hunter Syndrome Trial (ELAPRASE, Rituximab, Methotrexate)
Not yet recruiting
- Mucopolysaccharidosis (MPS)
- Hunter Syndrome
- ELAPRASE
- +3 more
- (no location specified)
Aug 8, 2022
Mucopolysaccharidosis II, MPS II Trial in United States (SB-913)
Terminated
- Mucopolysaccharidosis II
- MPS II
- SB-913
-
Oakland, California
- +4 more
Oct 21, 2022
Mucopolysaccharidosis II Trial in Salt Lake City, Fairfax (Genetic HMI-203)
Recruiting
- Mucopolysaccharidosis II
- Genetic HMI-203
-
Oakland, California
- +5 more
Jan 26, 2023
Mucopolysaccharidosis Type II Observational
Withdrawn
- Mucopolysaccharidosis II
- Observational
-
Oakland, California
- +2 more
Oct 6, 2022
Hunter Syndrome Trial in Lexington
Recruiting
- Hunter Syndrome
-
Lexington, MassachusettsShire
Nov 7, 2022
MPS I, MPS II, MPS IVA Trial in San Francisco (Aldurazyme (laronidase))
Recruiting
- MPS I
- +8 more
- Aldurazyme (laronidase)
-
San Francisco, CaliforniaUniversity of California
Apr 21, 2022
MPS (RaDiCo Cohort) (RaDiCo-MPS)
Recruiting
- Mucopolysaccharidosis I
- +7 more
-
Angers, France
- +22 more
Sep 12, 2023
Mucopolysaccharidosis Type I (MPS I), Hurler Syndrome, Hurler-Scheie Syndrome Trial in Orange, Philadelphia, Porto Alegre
Active, not recruiting
- Mucopolysaccharidosis Type I (MPS I)
- +2 more
- RGX-111
-
Orange, California
- +3 more
Jan 9, 2023
Mucopolysaccharidosis I, Mucopolysaccharidosis II, Mucopolysaccharidosis VI Trial in Torrance (Adalimumab Injection [Humira],
Recruiting
- Mucopolysaccharidosis I
- +2 more
- Adalimumab Injection [Humira]
- Saline Solution for Injection
-
Torrance, CaliforniaThe Lundquist Institute at Harbor-UCLA Medical Center
Aug 9, 2022
Mucopolysaccharidosis II, Hunter Syndrome Trial in Pusan, Seoul (GC1123)
Not yet recruiting
- Mucopolysaccharidosis II
- Hunter Syndrome
- GC1123
-
Pusan, Korea, Republic of
- +2 more
Jun 16, 2022
MPS IIIA, Sanfilippo Syndrome, Sanfilippo A Trial in Australia, Spain, United States (ABO-102)
Active, not recruiting
- MPS IIIA
- +3 more
- ABO-102
-
Columbus, Ohio
- +4 more
Nov 8, 2022
Neurodevelopmental Status in Pediatric Hunter Syndrome (MPS II)
Completed
- Mucopolysaccharidosis (MPS)
- Hunter Syndrome
-
Oakland, California
- +6 more
Mar 15, 2021
Mucopolysaccharidosis II Trial in Worldwide (Iduronate-2-sulfatase enzyme replacement therapy, iduronate-2-sulfatase enzyme
Completed
- Mucopolysaccharidosis II
- Iduronate-2-sulfatase enzyme replacement therapy
- +2 more
-
Oakland, California
- +8 more
May 30, 2021
Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)
Terminated
- Mucopolysaccharidosis Type 3 B
- rAAV9.CMV.hNAGLU
-
Columbus, Ohio
- +3 more
Apr 29, 2022
The Natural History of Metachromatic Leukodystrophy
Recruiting
- MLD
- +26 more
- Palliative Care
- Hematopoetic Stem Cell Transplantation
-
Pittsburgh, PennsylvaniaThe Program for the Study of Neurodevelopment in Rare Disorders,
Nov 2, 2021
Myozyme® and of Aldurazyme® in Male and Female Participants of
Recruiting
- Pompe Disease
- Mucopolysaccharidosis Type I (MPS I)
-
Italy, ItalyInvestigational site Italy
May 3, 2022
Hunter Syndrome, Mucopolysaccharidosis II, MPS II Trial in Porto Alegre, Warsaw, Taipei (Idursulfase)
Completed
- Hunter Syndrome
- +2 more
- Idursulfase
-
Porto Alegre, RS, Brazil
- +2 more
May 14, 2021
Mucopolysaccharidosis Type VI Trial in Naples, Ankara (AAV2/8.TBG.hARSB)
Active, not recruiting
- Mucopolysaccharidosis Type VI
- AAV2/8.TBG.hARSB
-
Naples, Italy
- +1 more
Nov 22, 2021
Mucopolysaccharidosis I, II, and VI Screening inHigh-Risk
Terminated
- Mucopolysaccharidosis (MPS)
-
Los Angeles, California
- +13 more
Mar 16, 2021